Tag Archives | enzyme replacement therapy

Gaucher’s Disease: An Overview

Gaucher’s disease is a rare lysosomal storage disorder that affects approximately 10,000 people worldwide. This disorder comes about when there aren’t enough glucocerebrosidase enzymes present to properly breakdown fat molecules and they begin to accumulate. This accumulation occurs within cell walls, and when it becomes too much, the cell swells to much larger than its […]

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