Survivors of Pompe Disease gathered at Duke University medical center to celebrate the success of drug trials that began in 2004. The drug that treats Pompe Disease – Myozyme – was developed at Duke and the trials began there. To read more about the reunion, please click here.
Tag Archives | Myozyme
Check out "Extraordinary Measures"
MEDICAL NEWS February 12, 2010
The movie “Extraordinary Measures” starring Harrison Ford and Brendan Fraser recounts the true story of one family’s search a treatment for Pompe Disease. Pompe Disease is a neuromuscular disorder that effects less than 10,000 people in the world. Today the lysosomal storage disorder can be treated with Myozyme. People living with Pompe disease lack the […]